Mindzilla – Duchenne Muscular Dystrophy

Researchers Developing New ‘DNA Stitch’ to Treat Muscular Dystrophy

September 26, 2019
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Edmonton, AB — A new therapeutic being tested by University of Alberta researchers is showing early promise as a more effective treatment that could help nearly half of patients with Duchenne muscular...

New Method to Boost CRISPR Efficiency Developed

March 6, 2019
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Dallas, TX — Scientists have developed a method to boost the efficiency of CRISPR gene editing in Duchenne muscular dystrophy (DMD), according to a study that could have implications for optimizing...

Single CRISPR Treatment Provides Long-Term Benefits in Mice

February 18, 2019
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Durham, N.C. — Researchers at Duke University have shown that a single systemic treatment using CRISPR genome editing technology can safely and stably correct a genetic disease — Duchenne muscular...

New Research Insights Hold Promise for Kids with DMD

February 11, 2019
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Washington, DC — Prednisone, the current standard of care used to treat kids with Duchenne muscular dystrophy (DMD), reduces chronic inflammation but has harsh side effects. Eplerenone, a heart failure...

Research Reveals Muscle Stem Cells Can Drive Cancer that Arises in Duchenne Muscular Dystrophy

January 16, 2019
Mindzilla

La Jolla, CA — People with Duchenne muscular dystrophy (DMD) can develop an otherwise-rare muscle cancer, called rhabdomyosarcoma, due to the muscle cells’ continuous work to rebuild the damaged...

Human ‘Chimeric’ Cells Restore Crucial Protein in Duchenne Muscular Dystrophy

March 16, 2018
Mindzilla

Chicago, IL — Cells made by fusing a normal human muscle cell with a muscle cell from a person with Duchenne muscular dystrophy — a rare but fatal form of muscular dystrophy — were able to significantly...

Chronic Inflammation Plays Critical Role in Sustained Delivery of New MD Therapy, Says Study

October 17, 2017
Mindzilla

Washington, DC — Macrophages, a type of white blood cell involved in inflammation, readily take up a newly approved medication for Duchenne muscular dystrophy (DMD) and promote its sustained delivery...

‘CRISPR-Gold’ Fixes Duchenne Muscular Dystrophy Mutation in Mice

October 4, 2017
Mindzilla

Berkeley, CA — Scientists at the University of California, Berkeley, have engineered a new way to deliver CRISPR-Cas9 gene-editing technology inside cells and have demonstrated in mice that the technology...