Mindzilla – Gene Therapy

Gene Therapy

Scientists Use Nanoparticle-Delivered Gene Therapy to Inhibit Blinding Eye Disease in Rodents

July 9, 2020
Mindzilla

Bethesda, MD — In experiments in rats and mice, two Johns Hopkins scientists — an engineer and an ophthalmologist — report the successful use of nanoparticles to deliver gene therapy for...

Critical Window for Re-Infection With HIV After Stem Cell Transplantation

May 15, 2020
Mindzilla

Heidelberg, Germany — Some people with HIV need to undergo an allogeneic stem cell transplantation in order to treat different types of blood cancer. Most of the patient’s immune cells are eliminated...

Study Shows Glaucoma Could Be Successfully Treated With Gene Therapy

April 22, 2020
Mindzilla

Bristol, UK — A new study led by the University of Bristol has shown a common eye condition, glaucoma, could be successfully treated with a single injection using gene therapy, which would improve...

Simulations Show How to Make Gene Therapy more Effective

April 20, 2020
Mindzilla

Groningen, Netherlands — Diseases with a genetic cause could, in theory, be treated by supplying a correct version of the faulty gene. However, in practice, delivering new genetic material to human...

Gene Therapy Generates New Neurons to Treat Huntington’s Disease

March 3, 2020
Mindzilla

Guangdong Province, China — Huntington’s disease (HD) is a rare disease characterized by abnormal chorea movement and caused by Huntingtin (Htt) gene mutation and neurodegeneration in a brain...

Gene Therapy/Gene Editing Combo could Offer Hope for some Genetic Disorders

February 13, 2020
Mindzilla

Washington, DC — A hybrid approach that combines elements of gene therapy with gene editing converted an experimental model of a rare genetic disease into a milder form, significantly enhancing survival,...

Novel Techniques for Mining Patented Gene Therapies Offer Promising Treatment Options

February 10, 2020
Mindzilla

West Lafayette, IN — The global gene therapy market is expected to reach $13 billion by 2024 as new treatment options target cancers and other diseases. Now, a team of scientists from Purdue University...

Six Patients With Rare Blood Disease Are Doing Well After Gene Therapy Clinical Trial

January 29, 2020
Mindzilla

Los Angeles, CA — UCLA researchers are part of an international team that reported the use of a stem cell gene therapy to treat nine people with the rare, inherited blood disease known as X-linked...

Nanoparticles Deliver ‘Suicide Gene’ Therapy to Paediatric Brain Tumours Growing in Mice

January 9, 2020
Helen Yiu

Baltimore, MD — Johns Hopkins researchers report that a type of biodegradable, lab-engineered nanoparticle they fashioned can successfully deliver a “suicide gene” to paediatric brain tumour...

Researchers Solve Protein Structure Associated with Inherited Retinal Diseases

January 9, 2020
Mindzilla

Durham, NH — Researchers at the University of New Hampshire have reported the first structural model for a key enzyme, and its activating protein, that can play a role in some genetically inherited...

Gene Therapy Shown to Offer Long-Term Benefits for People with Haemophilia A

January 7, 2020
Mindzilla

London, UK — A breakthrough gene therapy treatment for Haemophilia A has been shown to offer long-term benefits that have already transformed the lives of 13 men in the UK. Clinical researchers...

Using Gene Therapy to Treat Chronic Traumatic Encephalopathy

January 6, 2020
Mindzilla

New Rochelle, NY — A new study shows the feasibility of using gene therapy to treat the progressive neurodegenerative disorder chronic traumatic encephalopathy (CTE). The study, which demonstrated...

New Gene Therapy Strategy, Courtesy of Mother Nature

December 17, 2019
Mindzilla

Columbus, OH — Scientists have developed a new gene-therapy technique by transforming human cells into mass producers of tiny nano-sized particles full of genetic material that has the potential to...

Gene Therapy: Development of New DNA Transporters

November 19, 2019
Mindzilla

Halle, Germany — Scientists at the Institute of Pharmacy at Martin Luther University Halle-Wittenberg (MLU) have developed new delivery vehicles for future gene therapies. A team of researchers led...

Gene Therapy Helps Functional Recovery After Stroke

September 12, 2019
Mindzilla

A new gene therapy turns glial cells–abundant support cells in the brain–into neurons, repairing damage that results from stroke and significantly improving motor function in mice. A paper...

Research Team Used Genome Editing to Correct Two Mutations Associated with Cystic Fibrosis

August 7, 2019
Mindzilla

Italy — The approach adopted by the team of the University of Trento, led by Anna Cereseto, opens new perspectives in the treatment of cystic fibrosis, a genetic disease for which no cure is currently...

Proposed Gene Therapy for a Heart Arrhythmia, Based on Models Made from Patient Cells

July 17, 2019
Mindzilla

Boston, MA — Researchers at Boston Children’s Hospital report creating the first human tissue model of an inherited heart arrhythmia, replicating two patients’ abnormal heart rhythms in...

These Molecules could Trap Viruses Inside Cell

April 8, 2019
Mindzilla

Viruses are often used as vehicles for delivery in gene therapy because they’re engineered not to damage the cell once they get there, but neglecting to consider how the virus will exit the cell...

Gene Transfer Improves Diabetes-Linked Heart Ailment

March 28, 2019
Mindzilla

San Diego, CA — Researchers with the VA San Diego Healthcare System and the University of California San Diego have shown that a gene transfer technique can combat heart dysfunction caused by diabetes. Working...

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